Sarcoglycanopathies - 3 Studies Found
Completed |
: Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C :
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Completed |
: Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) : Muscular Dystrophies : 2007-06-27 :
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Enrolling by invitation |
: Gene Transfer Clinical Trial for LGMD2D (Alpha-sarcoglycan Deficiency) Using scAAVrh74.tMCK.hSGCA : Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) : 2013-07-24 : Drug: scAAVrh74.tMCK.hSGCA |