Paroxysmal Nocturnal Hemoglobinuria - 28 Studies Found
Active, not recruiting |
: Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry : Paroxysmal Nocturnal Hemoglobinuria : 2011-04-15 |
Completed |
: E07-001: Safety and Efficacy Extension Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients : Paroxysmal Nocturnal Hemoglobinuria : 2010-08-30 : Drug: Eculizumab Each vial contains 30 mL of 10 mg/mL eculizumab; dose of 900 mg intravenous every 14 da |
Completed |
: C07-001: Safety and Efficacy Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients : Paroxysmal Nocturnal Hemoglobinuria : 2010-08-30 : Biological: Eculizumab Subjects were treated with open label Eculizumab and following the dose described |
Active, not recruiting |
: An Open-Label, Intrapatient, Dose-Escalation Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of ALXN1210 Administered Intravenously to Patients With Paroxysmal Nocturnal Hemoglobinuria : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2015-11-02 :
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Recruiting |
: Proof of Concept Study to Assess the Efficacy, Safety and Pharmacokinetics of LFG316 in Patients With Paroxysmal Nocturnal Hemoglobinuria : Paroxysmal Nocturnal Hemoglobinuria PNH : 2015-08-07 : Biological: LFG316 LFG316 will be administered to all patients enrolled in the study |
Recruiting |
: Coversin in Paroxysmal Nocturnal Haemoglobinuria (PNH) : Paroxysmal Nocturnal Haemoglobinuria (PNH) : 2015-09-10 : Drug: Coversin Patients enrolled in this protocol will initially be treated with an ablating dose of Cov |
Terminated |
: Safety and Pharmacokinetics of TT30 in Subjects With Paroxysmal Nocturnal Hemoglobinuria (PNH) : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2011-04-12 :
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Recruiting |
: A Treatment Study of ACH-0144471 in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2017-02-01 : Drug: ACH-0144471 ACH-0144471 will be administered to all patients enrolled in the study. |
Not yet recruiting |
: ALXN1210 Versus Eculizumab in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Eculizumab : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2017-02-14 :
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Recruiting |
: ALXN1210 Versus Eculizumab in Complement Inhibitor Treatment-Naïve Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) : Paroxysmal Nocturnal Hemoglobinuria (PNH) : 2016-10-25 :
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